Invention Grant
- Patent Title: Compositions for modulating Ataxin 2 expression
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Application No.: US15127358Application Date: 2015-03-19
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Publication No.: US10308934B2Publication Date: 2019-06-04
- Inventor: Susan M. Freier
- Applicant: Ionis Pharmaceuticals, Inc.
- Applicant Address: US CA Carlsbad
- Assignee: Ionis Pharmaceuticals, Inc.
- Current Assignee: Ionis Pharmaceuticals, Inc.
- Current Assignee Address: US CA Carlsbad
- Agency: McNeill Baur PLLC
- International Application: PCT/US2015/021608 WO 20150319
- International Announcement: WO2015/143246 WO 20150924
- Main IPC: A61K48/00
- IPC: A61K48/00 ; C12N15/11 ; C12N15/113
Abstract:
Disclosed herein are antisense compounds and methods for decreasing Ataxin 2 mRNA and protein expression. Such methods, compounds, and compositions are useful to treat, prevent, or ameliorate Ataxin 2 associated diseases, disorders, and conditions. Such Ataxin 2 associated diseases include spinocerebellar ataxia type 2 (SCA2), amyotropic sclerosis (ALS), and parkinsonism.
Public/Granted literature
- US20170175114A1 COMPOSITIONS FOR MODULATING ATAXIN 2 EXPRESSION Public/Granted day:2017-06-22
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