Invention Grant
- Patent Title: Compositions for modulating expression of C9ORF72 antisense transcript
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Application No.: US15565838Application Date: 2015-04-16
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Publication No.: US10407678B2Publication Date: 2019-09-10
- Inventor: Frank Rigo
- Applicant: Ionis Pharmaceuticals, Inc.
- Applicant Address: US CA Carlsbad
- Assignee: Ionis Pharmaceuticals, Inc.
- Current Assignee: Ionis Pharmaceuticals, Inc.
- Current Assignee Address: US CA Carlsbad
- Agency: McNeill Baur PLLC
- International Application: PCT/US2015/026218 WO 20150416
- International Announcement: WO2016/167780 WO 20161020
- Main IPC: C12N15/113
- IPC: C12N15/113 ; C07H21/04 ; A61P25/28 ; A61P25/16 ; A61P21/00 ; C12N15/11
Abstract:
Disclosed herein are compositions and methods for modulating expression of C9ORF72 antisense transcript in a cell or animal with C9ORF72 antisense transcript specific inhibitors. Such methods are useful to treat, prevent, or ameliorate neurodegenerative diseases in an individual in need thereof. Such C9ORF72 antisense transcript specific inhibitors include antisense compounds.
Public/Granted literature
- US20180119142A1 COMPOSITIONS FOR MODULATING EXPRESSION OF C9ORF72 ANTISENSE TRANSCRIPT Public/Granted day:2018-05-03
Information query
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