Invention Grant
- Patent Title: Modified Friedreich ataxia genes and vectors for gene therapy
-
Application No.: US15340721Application Date: 2016-11-01
-
Publication No.: US10548947B2Publication Date: 2020-02-04
- Inventor: Richard J. Samulski
- Applicant: Bamboo Therapeutics, Inc.
- Applicant Address: US NC Chapel Hill
- Assignee: Bamboo Therapeutics, Inc.
- Current Assignee: Bamboo Therapeutics, Inc.
- Current Assignee Address: US NC Chapel Hill
- Main IPC: C12N15/09
- IPC: C12N15/09 ; C12N15/62 ; C12N15/63 ; C12N7/00 ; A61K48/00 ; A61K35/761 ; A61K39/235 ; A61K38/17 ; A61K35/76 ; C07K14/47
Abstract:
The present invention relates to a modified FXN gene providing for increased expression of the encoded protein frataxin that can be used for treatment of Friedreich ataxia.
Public/Granted literature
- US20170128528A1 MODIFIED FRIEDREICH ATAXIA GENES AND VECTORS FOR GENE THERAPY Public/Granted day:2017-05-11
Information query
IPC分类:
