Invention Grant
- Patent Title: Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
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Application No.: US15526690Application Date: 2015-11-13
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Publication No.: US10597660B2Publication Date: 2020-03-24
- Inventor: Dinah Wen-Yee Sah , Jinzhao Hou , Mathieu E. Nonnenmacher , Pengcheng Zhou , Markus Hossbach , Jochen Deckert
- Applicant: VOYAGER THERAPEUTICS, INC.
- Applicant Address: US MA Cambridge
- Assignee: VOYAGER THERAPEUTICS, INC.
- Current Assignee: VOYAGER THERAPEUTICS, INC.
- Current Assignee Address: US MA Cambridge
- Agency: DT Ward, PC
- Agent Donna T. Ward; Mark J. Hanson
- International Application: PCT/US2015/060562 WO 20151113
- International Announcement: WO2016/077687 WO 20160519
- Main IPC: C12N15/11
- IPC: C12N15/11 ; C12N15/113
Abstract:
The present invention relates to small interfering RNA (siRNA) molecules against the SOD1 gene, adeno-associated viral (AAV) vectors encoding siRNA molecules and methods for treating amyotrophic lateral sclerosis (ALS) using the siRNA molecules and AAV vectors.
Public/Granted literature
- US20180282732A1 COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS) Public/Granted day:2018-10-04
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