Invention Grant
- Patent Title: Method of treating mucopolysaccharidosis type I or II
-
Application No.: US14872537Application Date: 2015-10-01
-
Publication No.: US10648001B2Publication Date: 2020-05-12
- Inventor: Edward J. Rebar
- Applicant: Sangamo BioSciences, Inc.
- Applicant Address: US CA Richmond
- Assignee: Sangamo Therapeutics, Inc.
- Current Assignee: Sangamo Therapeutics, Inc.
- Current Assignee Address: US CA Richmond
- Agency: Pasternak Patent Law
- Main IPC: A01N63/00
- IPC: A01N63/00 ; C12N15/90 ; C12N9/22 ; A61K38/46 ; A61K38/47 ; A61K35/407 ; A61K48/00
Abstract:
Nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of a lysosomal storage disease.
Public/Granted literature
- US20160060656A1 METHODS AND COMPOSITIONS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES Public/Granted day:2016-03-03
Information query
