Invention Grant
- Patent Title: Antisense nucleic acids
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Application No.: US16717274Application Date: 2019-12-17
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Publication No.: US10683322B2Publication Date: 2020-06-16
- Inventor: Naoki Watanabe , Youhei Satou , Shin'ichi Takeda , Tetsuya Nagata
- Applicant: NIPPON SHINYAKU CO., LTD. , NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY
- Applicant Address: JP Kyoto-shi, Kyoto JP Kodaira-shi, Tokyo
- Assignee: NIPPON SHINYAKU CO., LTD.,NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY
- Current Assignee: NIPPON SHINYAKU CO., LTD.,NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY
- Current Assignee Address: JP Kyoto-shi, Kyoto JP Kodaira-shi, Tokyo
- Agency: Faegre Drinker Biddle & Reath LLP
- Priority: com.zzzhc.datahub.patent.etl.us.BibliographicData$PriorityClaim@25c6e416
- Main IPC: C12N15/11
- IPC: C12N15/11 ; C12N15/113 ; C07H21/00 ; C07H21/04 ; C12Q1/68

Abstract:
The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene. Also provided is a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency.
Public/Granted literature
- US20200109162A1 ANTISENSE NUCLEIC ACIDS Public/Granted day:2020-04-09
Information query
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