Invention Grant
- Patent Title: Gene therapy for treating hemophilia A
-
Application No.: US16691822Application Date: 2019-11-22
-
Publication No.: US10888628B2Publication Date: 2021-01-12
- Inventor: Lili Wang , James M. Wilson , Jenny Agnes Sidrane
- Applicant: The Trustees of the University of Pennsylvania
- Applicant Address: US PA Philadelphia
- Assignee: The Trustees of the University of Pennsylvania
- Current Assignee: The Trustees of the University of Pennsylvania
- Current Assignee Address: US PA Philadelphia
- Agency: Howson & Howson LLP
- Agent Colleen Schaller
- Main IPC: A61K48/00
- IPC: A61K48/00 ; C12N15/86 ; A61K9/00 ; A61P7/04 ; A61K38/37
Abstract:
Compositions and regimens useful in treating hemophilia A are provided. The compositions include recombinant adeno-associated virus (rAAV) with a transthyretin enhancer and promoter driving expression of a human Factor VIII.
Public/Granted literature
- US20200085975A1 GENE THERAPY FOR TREATING HEMOPHILIA A Public/Granted day:2020-03-19
Information query
