Invention Grant
- Patent Title: Exon skipping compositions for treating muscular dystrophy
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Application No.: US16220799Application Date: 2018-12-14
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Publication No.: US10907154B2Publication Date: 2021-02-02
- Inventor: Richard K. Bestwick , Diane Elizabeth Frank
- Applicant: Sarepta Therapeutics, Inc.
- Applicant Address: US MA Cambridge
- Assignee: Sarepta Therapeutics, Inc.
- Current Assignee: Sarepta Therapeutics, Inc.
- Current Assignee Address: US MA Cambridge
- Agency: Sterne, Kessler, Goldstein and Fox P.L.L.C.
- Main IPC: C12N15/11
- IPC: C12N15/11 ; C12N15/113 ; A61K47/60 ; A61K31/713 ; A61K47/64
Abstract:
Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 44 skipping are described.
Public/Granted literature
- US20190177724A1 EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY Public/Granted day:2019-06-13
Information query
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