Invention Grant
- Patent Title: Exon skipping oligomer conjugates for muscular dystrophy
-
Application No.: US16001310Application Date: 2018-06-06
-
Publication No.: US11000600B2Publication Date: 2021-05-11
- Inventor: Marco A. Passini , Gunnar J. Hanson
- Applicant: Sarepta Therapeutics, Inc.
- Applicant Address: US MA Cambridge
- Assignee: Sarepta Therapeutics, Inc.
- Current Assignee: Sarepta Therapeutics, Inc.
- Current Assignee Address: US MA Cambridge
- Agency: Sterne, Kessler, Goldstein & Fox P.L.L.C.
- Main IPC: A61K47/64
- IPC: A61K47/64 ; A61K47/54 ; A61P25/14 ; A61P21/00 ; A61K31/7088 ; A61K47/68
Abstract:
Antisense oligomer conjugates complementary to a selected target site in the human dystrophin gene to induce exon 53 skipping are described.
Public/Granted literature
- US20180271993A1 EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY Public/Granted day:2018-09-27
Information query
IPC分类:
