Invention Grant
- Patent Title: Methods and pharmaceutical composition for the treatment and the prevention of neurological phenotype associated with Friedreich ataxia
-
Application No.: US15560620Application Date: 2016-03-22
-
Publication No.: US11040113B2Publication Date: 2021-06-22
- Inventor: Hélène Puccio , Françoise Piguet
- Applicant: INSERM (INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE) , CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS) , UNIVERSITÉ DE STRASBOURG
- Applicant Address: FR Paris; FR Paris; FR Stasbourg
- Assignee: INSERM (INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE),CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS),UNIVERSITÉ DE STRASBOURG
- Current Assignee: INSERM (INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE),CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS),UNIVERSITÉ DE STRASBOURG
- Current Assignee Address: FR Paris; FR Paris; FR Stasbourg
- Agency: W&C IP
- Priority: EP15305420 20150323
- International Application: PCT/EP2016/056263 WO 20160322
- International Announcement: WO2016/150964 WO 20160929
- Main IPC: A61K48/00
- IPC: A61K48/00 ; C07K14/47 ; C12N15/86
Abstract:
The present invention relates to a vector which comprises a nucleic acid sequence encoding for the frataxin (FXN) gene for use in the prevention and treatment of neurological phenotype associated with Friedreich ataxia in a subject in need thereof.
Public/Granted literature
Information query
