Invention Grant
- Patent Title: Methods and compositions for treating urea cycle disorders
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Application No.: US17121639Application Date: 2020-12-14
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Publication No.: US11266655B2Publication Date: 2022-03-08
- Inventor: Alfica Sehgal , Alla A. Sigova , Igor Zlobine , Brian E. Schwartz , David A. Bumcrot , Vaishnavi Rajagopal , Yun Joon Jung , Yuichi Nishi
- Applicant: Camp4 Therapeutics Corporation
- Applicant Address: US MA Cambridge
- Assignee: Camp4 Therapeutics Corporation
- Current Assignee: Camp4 Therapeutics Corporation
- Current Assignee Address: US MA Cambridge
- Agency: Goodwin Procter LLP
- Main IPC: A61K31/5377
- IPC: A61K31/5377 ; A61K31/395 ; A61K31/416 ; A61K31/519 ; A61K31/52 ; C12N5/071

Abstract:
Provided are methods and compositions for the treating a patient with a urea cycle disorder. Methods and compositions are also provided for modulating genes encoding enzymes that participate in the urea cycle by altering gene signaling networks.
Public/Granted literature
- US20210114996A1 METHODS AND COMPOSITIONS FOR TREATING UREA CYCLE DISORDERS Public/Granted day:2021-04-22
Information query
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