Invention Grant
- Patent Title: Adenoassociated virus vectors for the treatment of mucopolysaccharidoses
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Application No.: US16337953Application Date: 2017-09-22
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Publication No.: US11338046B2Publication Date: 2022-05-24
- Inventor: Carles Roca Lecha , Virginia A. Haurigot-Mendonça , Fàtima Bosch Tubert
- Applicant: ESTEVE PHARMACEUTICALS, S.A. , UNIVERSITAT AUTÓNOMA DE BARCELONA
- Applicant Address: ES Barcelona; ES Cerdanyola del Valles
- Assignee: ESTEVE PHARMACEUTICALS, S.A.,UNIVERSITAT AUTÓNOMA DE BARCELONA
- Current Assignee: ESTEVE PHARMACEUTICALS, S.A.,UNIVERSITAT AUTÓNOMA DE BARCELONA
- Current Assignee Address: ES Barcelona; ES Cerdanyola del Valles
- Agency: Hueschen and Sage
- Priority: EP16382450 20160930
- International Application: PCT/EP2017/074081 WO 20170922
- International Announcement: WO2018/060097 WO 20180405
- Main IPC: A61K48/00
- IPC: A61K48/00 ; A61K38/46 ; A61P3/00 ; C12N15/86 ; C12N9/16

Abstract:
The present invention provides new adeno-associated virus-derived vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type IIID.
Public/Granted literature
- US20190231900A1 ADENOASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSES Public/Granted day:2019-08-01
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