Invention Grant
- Patent Title: Exon skipping oligomer conjugates for muscular dystrophy
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Application No.: US16938274Application Date: 2020-07-24
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Publication No.: US11491238B2Publication Date: 2022-11-08
- Inventor: Richard K. Bestwick , Frederick Joseph Schnell
- Applicant: Sarepta Therapeutics, Inc.
- Applicant Address: US MA Cambridge
- Assignee: Sarepta Therapeutics, Inc.
- Current Assignee: Sarepta Therapeutics, Inc.
- Current Assignee Address: US MA Cambridge
- Agency: Sterne, Kessler, Goldstein & Fox P.L.L.C.
- Main IPC: C07H21/04
- IPC: C07H21/04 ; A61K47/68 ; A61K9/00 ; C07K14/47 ; C12N15/113 ; C12N15/62
Abstract:
Antisense oligomers complementary to a selected target site in the human dystrophin gene to induce exon 52 skipping are described.
Public/Granted literature
- US20210138078A1 EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY Public/Granted day:2021-05-13
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