Invention Grant
- Patent Title: Treatment of glycogen storage disease III
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Application No.: US16491623Application Date: 2018-03-09
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Publication No.: US11541131B2Publication Date: 2023-01-03
- Inventor: Federico Mingozzi , Giuseppe Ronzitti , Patrice Vidal
- Applicant: GENETHON , UNIVERSITE D'EVRY VAL D'ESSONNE , INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE , SORBONNE UNIVERSITÉ
- Applicant Address: FR Evry; FR Evry; FR Paris; FR Paris
- Assignee: GENETHON,UNIVERSITE D'EVRY VAL D'ESSONNE,INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE,SORBONNE UNIVERSITÉ
- Current Assignee: GENETHON,UNIVERSITE D'EVRY VAL D'ESSONNE,INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE,SORBONNE UNIVERSITÉ
- Current Assignee Address: FR Evry; FR Evry; FR Paris; FR Paris
- Agency: Saliwanchik, Lloyd & Eisenschenk
- Priority: EP17305261 20170310
- International Application: PCT/EP2018/055976 WO 20180309
- International Announcement: WO2018/162748 WO 20180913
- Main IPC: A61K48/00
- IPC: A61K48/00 ; C07H21/04 ; C12N15/00 ; C12N15/63 ; C12N7/00 ; A61P3/08 ; C12N9/16

Abstract:
The present invention relates to vectors and compositions for the treatment of glycogen storage disease III.
Public/Granted literature
- US20200289673A1 TREATMENT OF GLYCOGEN STORAGE DISEASE III Public/Granted day:2020-09-17
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