Invention Grant
- Patent Title: Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
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Application No.: US17143036Application Date: 2021-01-06
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Publication No.: US11542506B2Publication Date: 2023-01-03
- Inventor: Dinah Wen-Yee Sah , Jinzhao Hou , Mathieu E. Nonnenmacher , Pengcheng Zhou , Markus Hossbach , Jochen Deckert
- Applicant: VOYAGER THERAPEUTICS, INC.
- Applicant Address: US MA Cambridge
- Assignee: VOYAGER THERAPEUTICS, INC.
- Current Assignee: VOYAGER THERAPEUTICS, INC.
- Current Assignee Address: US MA Cambridge
- Agency: Nelson Mullins Riley & Scarborough LLP
- Agent Jane E. Remillard, Esq.; Cynthia L. Kanik
- Main IPC: C12N15/11
- IPC: C12N15/11 ; C12N15/113
Abstract:
The present invention relates to small interfering RNA (siRNA) molecules against the SOD1 gene, adeno-associated viral (AAV) vectors encoding siRNA molecules and methods for treating amyotrophic lateral sclerosis (ALS) using the siRNA molecules and AAV vectors.
Public/Granted literature
- US20210139915A1 COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS) Public/Granted day:2021-05-13
Information query
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