Anc80 encoding sphingolipid-metabolizing proteins for mitigating disease-induced tissue damage
Abstract:
The present disclosure relates generally to the use of sphingolipid-metabolizing proteins to mitigate or minimize tissue damage resulting from injury or from disease, for example, pulmonary arterial hypertension (PAH) when the sphingolipid-metabolizing protein is delivered via expression from an Anc80 vector.
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