Invention Grant
- Patent Title: Exon skipping oligomer conjugates for muscular dystrophy
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Application No.: US17736148Application Date: 2022-05-04
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Publication No.: US11642364B2Publication Date: 2023-05-09
- Inventor: Marco A. Passini , Gunnar J. Hanson
- Applicant: Sarepta Therapeutics, Inc.
- Applicant Address: US MA Cambridge
- Assignee: Sarepta Therapeutics, Inc.
- Current Assignee: Sarepta Therapeutics, Inc.
- Current Assignee Address: US MA Cambridge
- Agency: Sterne, Kessler, Goldstein Fox
- Main IPC: A61K31/712
- IPC: A61K31/712 ; A61K31/7125 ; A61P21/00 ; C12N15/113 ; A61K47/64
Abstract:
Antisense oligomer conjugates complementary to a selected target site in the human dystrophin gene to induce exon 51 skipping are described.
Public/Granted literature
- US20220280546A1 EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY Public/Granted day:2022-09-08
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