Invention Grant
- Patent Title: Methods for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need thereof
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Application No.: US14903477Application Date: 2014-07-08
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Publication No.: US11667913B2Publication Date: 2023-06-06
- Inventor: Jean-Michel Rozet , Isabelle Perrault , Xavier Gerard , Josseline Kaplan , Arnold Munnich
- Applicant: INSERM (INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE) , FONDATION IMAGINE , UNIVERSITE PARIS DESCARTES , ASSISTANCE PUBLIQUE-HOPITAUX DE PARIS (APHP)
- Applicant Address: FR Paris
- Assignee: INSERM,FONDATION IMAGINE,UNIVERSITE PARIS CITE,ASSISTANCE PUBLIQUE-HÔPITAUX DE PARIS (APHP)
- Current Assignee: INSERM,FONDATION IMAGINE,UNIVERSITE PARIS CITE,ASSISTANCE PUBLIQUE-HÔPITAUX DE PARIS (APHP)
- Current Assignee Address: FR Paris; FR Paris; FR Paris; FR Paris
- Agency: WC&F IP
- Priority: EP 305968 2013.07.08
- International Application: PCT/EP2014/064604 2014.07.08
- International Announcement: WO2015/004133A 2015.01.15
- Date entered country: 2016-01-07
- Main IPC: C12N15/113
- IPC: C12N15/113 ; A61K48/00 ; C12N15/11
Abstract:
The present invention relates to methods for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need thereof. In particular, the present invention relates to a method for performing antisense oligonucleotide-mediated exon skipping in a retina cell of a subject comprising the step of injecting into the vitreous of the subject an amount of the antisense oligonucleotide.
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