Invention Grant
- Patent Title: Modulation of GYS1 expression
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Application No.: US17561095Application Date: 2021-12-23
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Publication No.: US11713462B2Publication Date: 2023-08-01
- Inventor: Tamar R. Grossman , Susan M. Freier , Berge Minassian , Saija Ahonen
- Applicant: Ionis Pharmaceuticals, Inc. , The Hospital for Sick Children
- Applicant Address: US CA Carlsbad
- Assignee: Ionis Pharmaceuticals, Inc.,The Hospital for Sick Children
- Current Assignee: Ionis Pharmaceuticals, Inc.,The Hospital for Sick Children
- Current Assignee Address: US CA Carlsbad; CA Toronto
- Agency: Michael Best & Friedrich LLP
- The original application number of the division: US16306831
- Main IPC: C07H21/02
- IPC: C07H21/02 ; C07H21/04 ; C12N15/113 ; A61K31/7088 ; A61K45/06 ; A61P3/08 ; A61P25/28
Abstract:
Provided herein are methods, compounds, and compositions for reducing expression of GYS1 in an individual. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate a glycogen storage disease or disorder in an individual in need.
Public/Granted literature
- US20220112502A1 MODULATION OF GYS1 EXPRESSION Public/Granted day:2022-04-14
Information query
