Invention Grant
US08632765B2 Modified factor VIII and factor IX genes and vectors for gene therapy
有权
修饰因子VIII和因子IX基因和基因治疗载体
- Patent Title: Modified factor VIII and factor IX genes and vectors for gene therapy
- Patent Title (中): 修饰因子VIII和因子IX基因和基因治疗载体
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Application No.: US13494068Application Date: 2012-06-12
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Publication No.: US08632765B2Publication Date: 2014-01-21
- Inventor: Richard J. Samulski
- Applicant: Richard J. Samulski
- Applicant Address: US NC Chapel Hill
- Assignee: Asklepios Biopharmaceuticals, Inc.
- Current Assignee: Asklepios Biopharmaceuticals, Inc.
- Current Assignee Address: US NC Chapel Hill
- Agency: Moore & Van Allen, PLLC
- Agent Marianne Fuierer
- Main IPC: A01N63/00
- IPC: A01N63/00 ; C07H21/02 ; C12N15/00

Abstract:
The present invention relates to a modified and optimized Factor VIII or Factor IX nucleic acid for inclusion in a chimeric virus vector. Use of such vector can be used for treatment of hemophilia.
Public/Granted literature
- US20130004462A1 MODIFIED FACTOR VIII AND FACTOR IX GENES AND VECTORS FOR GENE THERAPY Public/Granted day:2013-01-03
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