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US08633221B2 Method of enhancing lysosomal α-galactosidase A 有权
增强溶酶体α-半乳糖苷酶A的方法

Method of enhancing lysosomal α-galactosidase A
Abstract:
A method of enhancing the activity of lysosomal α-Galactosidase A (α-Gal A) in mammalian cells and for treatment of Fabry disease by administration of 1-deoxy-galactonojirimycin and related compounds.
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