Invention Grant
- Patent Title: Methods for treating Friedreich's ataxia with interferon gamma
- Patent Title (中): 用干扰素γ治疗弗里德里希共济失调的方法
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Application No.: US13820092Application Date: 2011-08-30
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Publication No.: US08815230B2Publication Date: 2014-08-26
- Inventor: Roberto Testi , Barbara Tomassini
- Applicant: Roberto Testi , Barbara Tomassini
- Agency: Fenwick & West LLP
- International Application: PCT/IB2011/002710 WO 20110830
- International Announcement: WO2012/028961 WO 20120308
- Main IPC: A61K38/21
- IPC: A61K38/21 ; A61K38/00 ; C07K14/57

Abstract:
Described herein are compositions and methods for treating Friedreich's Ataxia (FRDA) with interferon gamma. In some aspects, methods for increasing expression of frataxin in cells and for treating Friedreich's Ataxia are provided. In some additional aspects, methods increasing aconitase activity in cells are provided.
Public/Granted literature
- US20130156734A1 Compositions and Methods for Treating Friedreich's Ataxia with Interferon Gamma Public/Granted day:2013-06-20
Information query
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