Invention Grant
- Patent Title: Methods for treating lysosomal acid lipase deficiency
- Patent Title (中): 溶酶体酸性脂肪酶缺乏症的治疗方法
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Application No.: US13967050Application Date: 2013-08-14
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Publication No.: US08945542B2Publication Date: 2015-02-03
- Inventor: Michael Heartlein , Michael Concino , Paolo Martini , Muthuraman Meiyappan , Pericles Calias , Alla Romashko , Brian Pescatore , Lawrence Charnas , Jan Powell , Brian Felice , Nancy Savioli
- Applicant: Synageva Biopharma Corp.
- Applicant Address: US MA Lexington
- Assignee: Synageva Biopharma Corp.
- Current Assignee: Synageva Biopharma Corp.
- Current Assignee Address: US MA Lexington
- Agency: McDermott Will & Emery LLP
- Main IPC: A61K38/46
- IPC: A61K38/46
Abstract:
The present invention provides compositions and methods for effective treatment of a lysosomal acid lipase deficiency (LALD) disease, in particular, Wolman's disease and Cholesteryl Ester Storage Disease (CESD). Among other things, the present invention provides a method of treating developmental impairment or malnutrition in an individual suffering from a lysosomal acid lipase deficiency (LALD) disease, comprising administering to the individual a therapeutic effective amount of a lysosomal acid lipase.
Public/Granted literature
- US20140044697A1 METHODS FOR TREATING LYSOSOMAL ACID LIPASE DEFICIENCY Public/Granted day:2014-02-13
Information query
IPC分类:
