Invention Grant
US09226976B2 RAAV-based compositions and methods for treating alpha-1 anti-trypsin deficiencies
有权
用于治疗α-1抗胰蛋白酶缺乏症的基于RAAV的组合物和方法
- Patent Title: RAAV-based compositions and methods for treating alpha-1 anti-trypsin deficiencies
- Patent Title (中): 用于治疗α-1抗胰蛋白酶缺乏症的基于RAAV的组合物和方法
-
Application No.: US14113118Application Date: 2012-04-20
-
Publication No.: US09226976B2Publication Date: 2016-01-05
- Inventor: Terence Flotte , Christian Mueller
- Applicant: Terence Flotte , Christian Mueller
- Applicant Address: US MA Boston
- Assignee: University of Massachusetts
- Current Assignee: University of Massachusetts
- Current Assignee Address: US MA Boston
- Agency: Wolf, Greenfield & Sacks, P.C.
- International Application: PCT/US2012/034446 WO 20120420
- International Announcement: WO2012/145624 WO 20121026
- Main IPC: C07H21/02
- IPC: C07H21/02 ; C07H21/04 ; A61K48/00 ; A61K35/00 ; C12N15/67 ; C12N15/11
Abstract:
The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).
Public/Granted literature
- US20140142161A1 RAAV-BASED COMPOSITIONS AND METHODS FOR TREATING ALPHA-1 ANTI-TRYPSIN DEFICIENCIES Public/Granted day:2014-05-22
Information query
