Invention Grant
- Patent Title: Multiple exon skipping compositions for DMD
- Patent Title (中): 用于DMD的多个外显子跳过组合物
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Application No.: US14852264Application Date: 2015-09-11
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Publication No.: US09434948B2Publication Date: 2016-09-06
- Inventor: Peter Sazani , Ryszard Kole
- Applicant: Sarepta Therapeutics, Inc.
- Applicant Address: US MA Cambridge
- Assignee: Sarepta Therapeutics, Inc.
- Current Assignee: Sarepta Therapeutics, Inc.
- Current Assignee Address: US MA Cambridge
- Agency: Nelson Mullins Riley & Scarborough LLP
- Agent Amy E. Mandragouras, Esq.; Ariana D. Harris
- Main IPC: C12N15/113
- IPC: C12N15/113 ; C12N15/11
Abstract:
Provided are antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping, and methods of use thereof to treat muscular dystrophy.
Public/Granted literature
- US20150376618A1 MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD Public/Granted day:2015-12-31
Information query
IPC分类:
