Invention Grant
- Patent Title: Multiple exon skipping compositions for DMD
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Application No.: US14857569Application Date: 2015-09-17
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Publication No.: US09447416B2Publication Date: 2016-09-20
- Inventor: Peter Sazani , Ryszard Kole
- Applicant: Sarepta Therapeutics, Inc.
- Applicant Address: US MA Cambridge
- Assignee: Sarepta Therapeutics, Inc.
- Current Assignee: Sarepta Therapeutics, Inc.
- Current Assignee Address: US MA Cambridge
- Agency: Nelson Mullins Riley & Scarborough LLP
- Agent Amy E. Mandragouras, Esq.; Ariana D. Harris
- Main IPC: C12N15/113
- IPC: C12N15/113 ; C12N15/11
Abstract:
Provided are antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping, and methods of use thereof to treat muscular dystrophy.
Public/Granted literature
- US20160002633A1 MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD Public/Granted day:2016-01-07
Information query
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