Invention Grant
US09533004B2 Treatment of dystrophin family related diseases by inhibition of natural antisense transcript to DMD family
有权
通过抑制DMD家族的天然反义转录物治疗肌营养不良蛋白家族相关疾病
- Patent Title: Treatment of dystrophin family related diseases by inhibition of natural antisense transcript to DMD family
- Patent Title (中): 通过抑制DMD家族的天然反义转录物治疗肌营养不良蛋白家族相关疾病
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Application No.: US14564315Application Date: 2014-12-09
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Publication No.: US09533004B2Publication Date: 2017-01-03
- Inventor: Joseph Collard , Olga Khorkova Sherman
- Applicant: CuRNA, Inc.
- Applicant Address: US FL Miami
- Assignee: CuRNA, Inc.
- Current Assignee: CuRNA, Inc.
- Current Assignee Address: US FL Miami
- Agency: CuRNA, Inc.
- Agent Monte R. Browder
- Main IPC: C07H21/02
- IPC: C07H21/02 ; C07H21/04 ; A61K31/713 ; C12N15/113
Abstract:
The present invention relates to antisense oligonucleotides that modulate the expression of and/or function of Dystrophin family, in particular, by targeting natural antisense polynucleotides of Dystrophin family. The invention also relates to the identification of these antisense oligonucleotides and their use in treating diseases and disorders associated with the expression of DMD family.
Public/Granted literature
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