Invention Grant
- Patent Title: siRNA compounds comprising terminal substitutions
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Application No.: US14451233Application Date: 2014-08-04
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Publication No.: US09701960B2Publication Date: 2017-07-11
- Inventor: Sharon Avkin-Nachum
- Applicant: Quark Pharmaceuticals, Inc.
- Applicant Address: US CA Fremont
- Assignee: Quark Pharmaceuticals, Inc.
- Current Assignee: Quark Pharmaceuticals, Inc.
- Current Assignee Address: US CA Fremont
- Agency: Nutter McClennen & Fish LLP
- Agent Konstantin Linnik
- Main IPC: C12N15/11
- IPC: C12N15/11 ; C12N15/113

Abstract:
The invention relates to modified siRNA compounds which down-regulate target gene expression, to pharmaceutical compositions comprising such compounds and to methods of treating and/or preventing the incidence or severity of various diseases or conditions associated with the genes and/or symptoms associated with such diseases or conditions.
Public/Granted literature
- US20150152412A1 SIRNA COMPOUNDS COMPRISING TERMINAL SUBSTITUTIONS Public/Granted day:2015-06-04
Information query
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