Invention Grant
- Patent Title: RAAV-based compositions and methods for treating alpha-1 anti-trypsin deficiencies
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Application No.: US14952217Application Date: 2015-11-25
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Publication No.: US09885057B2Publication Date: 2018-02-06
- Inventor: Terence Flotte , Christian Mueller , Phillip D. Zamore
- Applicant: University of Massachusetts
- Applicant Address: US MA Boston
- Assignee: University of Massachusetts
- Current Assignee: University of Massachusetts
- Current Assignee Address: US MA Boston
- Agency: Wolf, Greenfield & Sacks, P.C.
- Main IPC: C07H21/02
- IPC: C07H21/02 ; C07H21/04 ; A61K48/00 ; A61K35/00 ; C12N15/86 ; C12N7/00 ; C12N15/113 ; A61K35/12
Abstract:
The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).
Public/Granted literature
- US20170159071A9 RAAV-BASED COMPOSITIONS AND METHODS FOR TREATING ALPHA-1 ANTI-TRYPSIN DEFICIENCIES Public/Granted day:2017-06-08
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