Invention Grant
- Patent Title: CFTR corrector for the treatment of genetic disorders affecting striated muscle
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Application No.: US14647773Application Date: 2013-11-29
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Publication No.: US09987256B2Publication Date: 2018-06-05
- Inventor: Dorianna Sandona' , Roberta Sacchetto , Elisa Bianchini , Pompeo Volpe , Romeo Betto , Francesco Mascarello
- Applicant: UNIVERSITA' DEGLI STUDI DI PADOVA
- Applicant Address: IT Padova
- Assignee: UNIVERSITA' DEGLI STUDI DI PADOVA
- Current Assignee: UNIVERSITA' DEGLI STUDI DI PADOVA
- Current Assignee Address: IT Padova
- Agency: Silvia Salvadori, P.C.
- Agent Silvia Salvadori
- Priority: ITMI2012A002065 20121203
- International Application: PCT/EP2013/075158 WO 20131129
- International Announcement: WO2014/086687 WO 20140612
- Main IPC: A61K31/425
- IPC: A61K31/425 ; A61K31/426 ; A61K31/427 ; A61K31/496 ; A61K31/517 ; A61K31/404 ; A61K31/443 ; A61K31/47 ; A61K31/4709 ; A61K31/472 ; A61K31/506
Abstract:
The present invention relates to the use of CFTR correctors in the treatment of genetic disorders affecting striated muscle selected from sarcoglycanopathies, Brody's disease (BD) and the recessive forms of Cathecolaminergic Polymorphic Ventricular Tachycardia (CPVT).
Public/Granted literature
- US20150328217A1 A CFTR CORRECTOR FOR THE TREATMENT OF GENETIC DISORDERS AFFECTING STRIATED MUSCLE Public/Granted day:2015-11-19
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