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公开(公告)号:AU2003256755A8
公开(公告)日:2004-02-09
申请号:AU2003256755
申请日:2003-07-23
Applicant: PTC THERAPEUTICS INC
Inventor: HWANG SEONGWOO , CHEN GUANGMING , WILDE RICHARD G , TAKASUGI JAMES J , WELCH ELLEN M
IPC: A61K31/17 , A61K31/4166 , A61P35/00 , C07C275/42 , C07D233/32 , C07D233/42 , C07D233/70 , C07D233/72 , C07D233/78 , C07D233/84 , C07D285/16 , C07D401/04 , C07D401/10 , C07D405/04 , C07D405/06 , C07D409/04 , C07D409/10 , C07D403/10 , C07D285/06
Abstract: The invention encompasses ureido substituted benzoic acid compounds, compositions comprising the compounds and methods for treating or preventing diseases associated with nonsense mutations of mRNA by administering these compounds or compositions.
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公开(公告)号:ES2926542T3
公开(公告)日:2022-10-26
申请号:ES21169137
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL G , MOON YOUNG-CHOON
IPC: C07D271/06 , A61K31/4245 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
Abstract: En el presente documento se proporciona un compuesto de fórmula o una sal farmacéuticamente aceptable del mismo para usar en un método para tratar un trastorno de almacenamiento lisosomal asociado con un codón de terminación prematuro en un paciente. (Traducción automática con Google Translate, sin valor legal)
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公开(公告)号:PL3889142T3
公开(公告)日:2022-09-26
申请号:PL21169137
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY MITCHELL , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL G , MOON YOUNG-CHOON
IPC: A61K31/4245 , C07D271/06 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
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公开(公告)号:ES2881198T3
公开(公告)日:2021-11-29
申请号:ES19174887
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY MITCHELL , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL GREGORY , MOON YOUNG-CHOON
IPC: C07D271/06 , A61K31/4245 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
Abstract: Un compuesto de fórmula: **(Ver fórmula)** o una composición farmacéutica que comprende dicho compuesto para su uso en un método para tratar la ataxia- telangiectasia resultante de un codón de terminación prematuro en un paciente.
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公开(公告)号:LT3386511T
公开(公告)日:2021-08-25
申请号:LT16874024
申请日:2016-12-11
Applicant: PTC THERAPEUTICS INC
Inventor: BABU SURESH , BHATTACHARYYA ANURADHA , HWANG SEONGWOO , JANI MINAKSHI , MOON YOUNG-CHOON , SYDORENKO NADIYA
IPC: C07D403/12 , A61K31/501 , A61K31/506 , A61K31/517 , C07D237/20 , C07D401/14 , C07D403/10 , C07D405/12 , C07D413/14 , C07D417/12 , C07D417/14 , C07D471/10 , C07D487/10
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公开(公告)号:DK3549936T3
公开(公告)日:2021-07-12
申请号:DK19174887
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY MITCHELL , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL GREGORY , MOON YOUNG-CHOON
IPC: C07D271/06 , A61K31/4245 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
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公开(公告)号:ES2770035T3
公开(公告)日:2020-06-30
申请号:ES17204895
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL GREGORY , MOON YOUNG-CHOON
IPC: C07D271/06 , A61K31/4245 , A61P27/02 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
Abstract: Un compuesto de fórmula:**Fórmula** o una composición farmacéutica que comprende dicho compuesto para su uso en un método para tratar la retinitis pigmentosa resultante de un codón de terminación prematuro en un paciente.
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公开(公告)号:DK3345895T3
公开(公告)日:2020-02-03
申请号:DK17204895
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY MITCHELL , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL GREGORY , MOON YOUNG-CHOON
IPC: C07D271/06 , A61K31/4245 , A61P27/02 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
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公开(公告)号:PL3103800T3
公开(公告)日:2018-11-30
申请号:PL16170630
申请日:2004-04-09
Applicant: PTC THERAPEUTICS INC
Inventor: KARP GARY MITCHELL , HWANG SEONGWOO , CHEN GUANGMING , ALMSTEAD NEIL GREGORY , MOON YOUNG-CHOON
IPC: C07D271/06 , A61K31/4245 , A61P35/00 , C07D271/12 , C07D413/04 , C07D413/10
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公开(公告)号:SG11201804915RA
公开(公告)日:2018-07-30
申请号:SG11201804915R
申请日:2016-12-11
Applicant: PTC THERAPEUTICS INC
Inventor: BABU SURESH , BHATTACHARYYA ANURADHA , HWANG SEONGWOO , JANI MINAKSHI , MOON YOUNG-CHOON , SYDORENKO NADIYA
IPC: A61K31/506 , A61P25/00 , C07D405/12
Abstract: The present description relates to compounds, forms, and pharmaceutical compositions thereof and methods of using such compounds, forms, or compositions thereof for treating or ameliorating Huntington's disease.In particular, the present description relates to substituted monocyclic heteroaryl compounds of Formula (I), forms and pharmaceutical compositions thereof and methods of using such compounds, forms, or compositions thereof for treating or ameliorating Huntington's disease.
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