公开(公告)号：AU2023338957A1

公开(公告)日：2025-02-20

申请号：AU2023338957

申请日：2023-09-08

Applicant: VERTEX PHARMA

Inventor： ALLEN EMILY ELIZABETH ,  BOYD MICHAEL J ,  FIMOGNARI JR ,  GIROUX SIMON ,  GREY JR ,  LAI-CHEN MICHELLE ,  MEDEK ALES ,  LI MENGQI ,  POFF CHRISTOPHER DAVID ,  RICHTER DANIEL TYLER ,  SCOTT TONY Z ,  SOKOLOWSKY KATHLEEN PAIGE ,  SPERRY JEFFREY BRADEN ,  TSAY CHARLENE ,  WANG XIAOXU ,  ZAKY MARIAM ,  ZHANG CHENLONG ,  MAXWELL BRAD ,  GLADDING JEFFERY

IPC: C07D405/04 ,  A61K31/4162 ,  A61P1/16 ,  A61P11/00 ,  C07D487/04

Abstract: Novel compounds, compositions, and methods of using and preparing the same, which may be useful for treating alpha-1 antitrypsin deficiency (AATD). (Formula (I))